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Top 10 search results for "Zolgensma" in Resources. To see all results and access other features, sign up for free.

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SMA Medication Zolgensma May Cause Liver Failure, Warns New Label Update

Zolgensma (onasemnogene abeparvovec-xioi), a treatment for children with spinal muscular atrophy ...
Posted 11/30/2021

SMA Medication Zolgensma May Cause Liver Failure, Warns New Label Update

Zolgensma (onasemnogene abeparvovec-xioi), a treatment for children with spinal muscular atrophy ...
Posted 11/30/2021
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SMA Treatment for Children vs. Adults: 5 Key Differences

Spinal muscular atrophy (SMA) mainly affects children, but it doesn’t spare adults — 35 percent o...

SMA Treatment for Children vs. Adults: 5 Key Differences

Spinal muscular atrophy (SMA) mainly affects children, but it doesn’t spare adults — 35 percent o...
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Understanding How SMA Gene Therapy Works

When a child is born with spinal muscular atrophy (SMA), a rare neuromuscular disorder, it’s the ...

Understanding How SMA Gene Therapy Works

When a child is born with spinal muscular atrophy (SMA), a rare neuromuscular disorder, it’s the ...
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Spinraza Alone May Be Better Than Combining It With Zolgensma To Treat SMA Type 1

A recent study has found that combining Zolgensma and Spinraza does not improve motor or respirat...
Posted 02/23/2022

Spinraza Alone May Be Better Than Combining It With Zolgensma To Treat SMA Type 1

A recent study has found that combining Zolgensma and Spinraza does not improve motor or respirat...
Posted 02/23/2022
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Interview: Dr. Strober on Combination Therapy for Babies With SMA

Many parents of children with spinal muscular atrophy (SMA) have questions about combination ther...
Posted 09/21/2021

Interview: Dr. Strober on Combination Therapy for Babies With SMA

Many parents of children with spinal muscular atrophy (SMA) have questions about combination ther...
Posted 09/21/2021
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New Study: Zolgensma May Benefit Adults With SMA Types 2 and 3

Zolgensma, a formulation of onasemnogene abeparvovec-xioi, is a type of gene therapy that can hel...
Posted 11/16/2022

New Study: Zolgensma May Benefit Adults With SMA Types 2 and 3

Zolgensma, a formulation of onasemnogene abeparvovec-xioi, is a type of gene therapy that can hel...
Posted 11/16/2022
read more >

Treatment With Evrysdi After Zolgensma Shows Benefit for SMA Type 1

Researchers reviewed four cases in which children with spinal muscular atrophy (SMA) type 1 recei...
Posted 09/02/2021

Treatment With Evrysdi After Zolgensma Shows Benefit for SMA Type 1

Researchers reviewed four cases in which children with spinal muscular atrophy (SMA) type 1 recei...
Posted 09/02/2021
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Evrysdi Development Team Wins Drug Discovery Award for Oral SMA Treatment

The researchers who discovered and developed the spinal muscular atrophy (SMA) treatment Evrysdi...
Posted 03/09/2022

Evrysdi Development Team Wins Drug Discovery Award for Oral SMA Treatment

The researchers who discovered and developed the spinal muscular atrophy (SMA) treatment Evrysdi...
Posted 03/09/2022
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Spinal Muscular Atrophy Type 1

Spinal muscular atrophy (SMA) type 1 is the most common type of spinal muscular atrophy. SMA is a...

Spinal Muscular Atrophy Type 1

Spinal muscular atrophy (SMA) type 1 is the most common type of spinal muscular atrophy. SMA is a...
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The Role of SMN1 and SMN2 Genes in Spinal Muscular Atrophy

Parents of children with spinal muscular atrophy (SMA) must learn a lot very quickly. Genetics is...

The Role of SMN1 and SMN2 Genes in Spinal Muscular Atrophy

Parents of children with spinal muscular atrophy (SMA) must learn a lot very quickly. Genetics is...
read article >