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Top 10 search results for "Evrysdi" in Resources. To see all results and access other features, sign up for free.

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Evrysdi Development Team Wins Drug Discovery Award for Oral SMA Treatment

The researchers who discovered and developed the spinal muscular atrophy (SMA) treatment Evrysdi...
Posted 03/09/2022

Evrysdi Development Team Wins Drug Discovery Award for Oral SMA Treatment

The researchers who discovered and developed the spinal muscular atrophy (SMA) treatment Evrysdi...
Posted 03/09/2022
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More Than Half of People Who Start Spinraza for SMA Stop Within 2 Years, Study Finds

People who start taking Spinraza (nusinersen) to treat spinal muscular atrophy (SMA) may not alwa...
Posted 12/15/2021

More Than Half of People Who Start Spinraza for SMA Stop Within 2 Years, Study Finds

People who start taking Spinraza (nusinersen) to treat spinal muscular atrophy (SMA) may not alwa...
Posted 12/15/2021
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The Role of SMN1 and SMN2 Genes in Spinal Muscular Atrophy

Parents of children with spinal muscular atrophy (SMA) must learn a lot very quickly. Genetics is...

The Role of SMN1 and SMN2 Genes in Spinal Muscular Atrophy

Parents of children with spinal muscular atrophy (SMA) must learn a lot very quickly. Genetics is...
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The Importance of Splicing in SMA Treatment

Spinal muscular atrophy (SMA) is a genetic disease that destroys nerve cells in the spinal cord a...

The Importance of Splicing in SMA Treatment

Spinal muscular atrophy (SMA) is a genetic disease that destroys nerve cells in the spinal cord a...
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Spinal Muscular Atrophy Pathophysiology

The term “pathophysiology” refers to the abnormalities in the body that underlie or cause a disea...

Spinal Muscular Atrophy Pathophysiology

The term “pathophysiology” refers to the abnormalities in the body that underlie or cause a disea...
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Understanding How SMA Gene Therapy Works

When a child is born with spinal muscular atrophy (SMA), a rare neuromuscular disorder, it’s the ...

Understanding How SMA Gene Therapy Works

When a child is born with spinal muscular atrophy (SMA), a rare neuromuscular disorder, it’s the ...
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Treatment With Evrysdi After Zolgensma Shows Benefit for SMA Type 1

Researchers reviewed four cases in which children with spinal muscular atrophy (SMA) type 1 recei...
Posted 09/02/2021

Treatment With Evrysdi After Zolgensma Shows Benefit for SMA Type 1

Researchers reviewed four cases in which children with spinal muscular atrophy (SMA) type 1 recei...
Posted 09/02/2021
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Long-Term Data: Children With Type 1 SMA Keep Gaining Motor Skills After 3 Years on Evrysdi

New data shows that risdiplam (sold as Evrysdi) helps most infants with spinal muscular atrophy (...
Posted 06/15/2022

Long-Term Data: Children With Type 1 SMA Keep Gaining Motor Skills After 3 Years on Evrysdi

New data shows that risdiplam (sold as Evrysdi) helps most infants with spinal muscular atrophy (...
Posted 06/15/2022
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Interview: Dr. Strober on Combination Therapy for Babies With SMA

Many parents of children with spinal muscular atrophy (SMA) have questions about combination ther...
Posted 09/21/2021

Interview: Dr. Strober on Combination Therapy for Babies With SMA

Many parents of children with spinal muscular atrophy (SMA) have questions about combination ther...
Posted 09/21/2021
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How To Appeal an Insurance Company Denial for SMA

If you are living with spinal muscular atrophy (SMA), you’re likely aware of the high costs assoc...

How To Appeal an Insurance Company Denial for SMA

If you are living with spinal muscular atrophy (SMA), you’re likely aware of the high costs assoc...
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